Successful Treatment of Baby with Rare Genetic Disorder Using CRISPR Technology

Doctors have successfully treated a baby with a rare genetic disorder using CRISPR technology, potentially reversing his condition and reducing the risk of brain damage and death. The treatment opens doors for transformative personalized medicine for rare diseases.

Gene Therapy for Heart Failure

A new gene therapy has shown promising results in reversing heart failure in large animal studies, with potential to revolutionize heart failure treatments in humans in the future.

Experimental Gene Therapy for Herpes Virus Infections

Scientists in Seattle have developed an experimental gene therapy that showed promising results in eliminating up to 97% of herpes virus infections in mice. The therapy aims to surgically remove herpes DNA from nerve cells using gene editing molecules injected into the bloodstream.

Development of Human Artificial Chromosomes for Gene Therapy and Biotechnology Applications

Scientists at the University of Pennsylvania have developed a new method to create human artificial chromosomes (HACs) that could revolutionize gene therapy and biotechnology applications. Their approach efficiently forms single-copy HACs, overcoming a common hurdle in the field.