Challenges in Accessing Treatments for Rare Diseases

A man diagnosed with Duchenne muscular dystrophy at age 6 shares his fight for a cure while facing regulatory roadblocks that hinder access to potentially life-saving treatments. He advocates for legislation like the 'Right to Try for Individualized Treatments' to give patients and doctors more control over treatment decisions.

Innovative Awake Kidney Transplant Procedure

A man in Chicago received a kidney transplant while awake and went home the next day, marking it as an outpatient procedure. This innovative 'awake transplant' could reduce risks and increase access to care for patients.